2
Orphan Designations
1
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| WHIM syndrome 1 | Xolremdi | Orphan Designation | - |
| WHIM syndrome 2 | Xolremdi | Orphan Designation | - |
| Waldenstrom macroglobulinemia | mavorixafor | Orphan Designation | - |
| anogenital human papillomavirus infection | Xolremdi | Orphan Designation | - |
| common wart | Xolremdi | Orphan Designation | - |
| laryngeal papillomatosis | Xolremdi | Orphan Designation | - |
| lymphoplasmacytic lymphoma | mavorixafor | Orphan Designation | - |
| macroglobulinemia, Waldenstrom, 1 | mavorixafor | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 6 (hepatocerebral type) | Xolremdi | Orphan Designation | - |
| monosomy X | Xolremdi | Orphan Designation | - |
| neuronopathy, distal hereditary motor, autosomal recessive 10 | Xolremdi | Orphan Designation | - |