4
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Behcet disease | gevokizumab | Orphan Designation | - |
| bronchial endocrine tumor | gevokizumab | Orphan Designation | - |
| pyoderma gangrenosum | gevokizumab | Orphan Designation | - |
| recessive dystrophic epidermolysis bullosa-generalized other | gevokizumab | Orphan Designation | - |
| severe Canavan disease | Recombinant bactericidal/permeability-increasing protein | Orphan Designation | - |
| severe achondroplasia-developmental delay-acanthosis nigricans syndrome | Recombinant bactericidal/permeability-increasing protein | Orphan Designation | - |
| severe neonatal-onset encephalopathy with microcephaly | Recombinant bactericidal/permeability-increasing protein | Orphan Designation | - |
| thymic neuroendocrine tumor | gevokizumab | Orphan Designation | - |