1
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| X-linked myotubular myopathy | donor human lung graft rehabilitated through xenogeneic cross-circulation | Orphan Designation | - |
| toxic epidermal necrolysis | donor human lung graft rehabilitated through xenogeneic cross-circulation | Orphan Designation | - |