1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Char syndrome | Anatibant | Orphan Designation | - |
| H syndrome | Anatibant | Orphan Designation | - |
| midface hypoplasia, hearing impairment, elliptocytosis, and nephrocalcinosis | Anatibant | Orphan Designation | - |