4
Orphan Designations
0
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Muckle-Wells syndrome | Ethenesulfonamide, 2-[(2R)-1,2-dimethyl-2- pyrrolidinyl]-N-[[(1,2,3,5,6,7-hexahydro-s-indacen-4- yl)amino]carbonyl]-, (1E)- | Orphan Designation | - |
| Plasmodium vivax malaria | quinine sulfate | Orphan Designation | - |
| amyotrophic lateral sclerosis | usnoflast | Orphan Designation | - |
| cryopyrin-associated periodic syndrome | Ethenesulfonamide, 2-[(2R)-1,2-dimethyl-2- pyrrolidinyl]-N-[[(1,2,3,5,6,7-hexahydro-s-indacen-4- yl)amino]carbonyl]-, (1E)- | Orphan Designation | - |
| familial cold autoinflammatory syndrome 1 | Ethenesulfonamide, 2-[(2R)-1,2-dimethyl-2- pyrrolidinyl]-N-[[(1,2,3,5,6,7-hexahydro-s-indacen-4- yl)amino]carbonyl]-, (1E)- | Orphan Designation | - |
| malaria | quinine sulfate | Orphan Designation | - |
| mixed malaria | quinine sulfate | Orphan Designation | - |
| primary biliary cholangitis | saroglitazar magnesium | Orphan Designation | - |
| primary biliary cholangitis 1 | saroglitazar magnesium | Orphan Designation | - |
| primary biliary cholangitis 4 | saroglitazar magnesium | Orphan Designation | - |