4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
10 companies found
70 approved / 109 designated
23 approved / 67 designated
38 approved / 22 designated
18 designated · 0 approved
1 approved / 9 designated
8 designated · 0 approved
7 designated · 0 approved
7 approved / 2 designated
1 designated · 0 approved
3 approved / 1 designated