4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
7 companies found
70 approved / 109 designated
3 approved / 20 designated
1 approved / 11 designated
9 designated · 0 approved
37 approved / 2 designated
1 designated · 0 approved
1 designated · 0 approved