4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
18 companies found
10 approved / 43 designated
41 designated · 0 approved
6 approved / 29 designated
1 approved / 25 designated
19 designated · 0 approved
31 approved / 16 designated
10 designated · 0 approved
81 approved / 8 designated
3 approved / 5 designated
1 approved / 4 designated
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 approved / 1 designated