4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
7 companies found
70 approved / 109 designated
43 designated · 0 approved
41 designated · 0 approved
34 designated · 0 approved
38 approved / 34 designated
26 approved / 30 designated
9 approved / 24 designated