4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
9 companies found
47 approved / 88 designated
8 approved / 26 designated
23 designated · 0 approved
7 approved / 11 designated
10 designated · 0 approved
7 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
1 approved / 1 designated