4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
8 companies found
70 approved / 109 designated
47 approved / 88 designated
26 approved / 30 designated
6 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved