4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
10 companies found
29 approved / 42 designated
8 approved / 27 designated
9 designated · 0 approved
6 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 approved / 2 designated
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved