4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
6 companies found
18 designated · 0 approved
31 approved / 16 designated
15 approved / 11 designated
4 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved