4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
15 companies found
34 designated · 0 approved
5 approved / 28 designated
19 approved / 23 designated
2 approved / 13 designated
1 approved / 6 designated
4 approved / 6 designated
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
1 approved / 2 designated
1 approved / 2 designated
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved