4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
7 companies found
6 approved / 29 designated
8 approved / 27 designated
6 approved / 11 designated
6 designated · 0 approved
3 approved / 5 designated
2 designated · 0 approved
1 designated · 0 approved