4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
8 companies found
8 approved / 25 designated
19 designated · 0 approved
43 approved / 14 designated
6 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved