4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
23 companies found
14 approved / 34 designated
8 approved / 25 designated
9 approved / 24 designated
11 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
2 approved / 3 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved