4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
8 companies found
70 approved / 109 designated
8 approved / 25 designated
19 approved / 23 designated
15 designated · 0 approved
1 approved / 4 designated
4 approved / 3 designated
1 approved / 2 designated
1 designated · 0 approved