4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
34 companies found
70 approved / 109 designated
47 approved / 88 designated
41 designated · 0 approved
39 designated · 0 approved
5 approved / 28 designated
8 approved / 27 designated
9 approved / 24 designated
15 designated · 0 approved
17 approved / 13 designated
12 designated · 0 approved
2 approved / 7 designated
6 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved