4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
6 companies found
29 approved / 42 designated
6 approved / 29 designated
15 designated · 0 approved
15 approved / 11 designated
1 designated · 0 approved
1 approved / 1 designated