4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
14 companies found
70 approved / 109 designated
34 approved / 57 designated
26 approved / 30 designated
6 approved / 29 designated
9 approved / 24 designated
3 approved / 15 designated
13 designated · 0 approved
3 approved / 5 designated
4 designated · 0 approved
6 approved / 4 designated
3 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved