4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
38 companies found
70 approved / 109 designated
34 approved / 57 designated
10 approved / 43 designated
29 approved / 42 designated
41 designated · 0 approved
9 approved / 24 designated
23 designated · 0 approved
13 designated · 0 approved
17 approved / 13 designated
9 approved / 7 designated
6 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
8 approved / 5 designated
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 approved / 2 designated
2 designated · 0 approved