4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
29 companies found
41 designated · 0 approved
34 designated · 0 approved
38 approved / 34 designated
14 approved / 34 designated
8 approved / 27 designated
1 approved / 25 designated
19 approved / 23 designated
8 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved