4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
93 companies found
47 approved / 88 designated
34 designated · 0 approved
26 approved / 30 designated
8 approved / 25 designated
2 approved / 23 designated
38 approved / 22 designated
18 designated · 0 approved
15 designated · 0 approved
4 approved / 12 designated
11 designated · 0 approved
5 approved / 8 designated
2 approved / 7 designated
1 approved / 6 designated
6 designated · 0 approved
6 designated · 0 approved
1 approved / 5 designated
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved