4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
9 companies found
70 approved / 109 designated
43 designated · 0 approved
39 designated · 0 approved
6 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved