4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
16 companies found
34 approved / 57 designated
29 approved / 42 designated
8 approved / 25 designated
23 designated · 0 approved
18 designated · 0 approved
15 designated · 0 approved
11 approved / 14 designated
1 approved / 6 designated
4 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved