4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
7 companies found
70 approved / 109 designated
23 approved / 67 designated
19 designated · 0 approved
13 designated · 0 approved
5 designated · 0 approved
3 designated · 0 approved
1 designated · 0 approved