4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
8 companies found
70 approved / 109 designated
5 approved / 14 designated
2 approved / 10 designated
5 designated · 0 approved
7 approved / 4 designated
3 designated · 0 approved
4 approved / 1 designated
1 designated · 0 approved