4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
80 companies found
70 approved / 109 designated
47 approved / 88 designated
23 approved / 67 designated
43 designated · 0 approved
10 approved / 43 designated
41 designated · 0 approved
39 designated · 0 approved
34 designated · 0 approved
14 approved / 34 designated
38 approved / 34 designated
32 approved / 30 designated
6 approved / 29 designated
5 approved / 28 designated
8 approved / 27 designated
1 approved / 25 designated
9 approved / 24 designated
23 designated · 0 approved
38 approved / 22 designated
3 approved / 20 designated
19 designated · 0 approved
31 approved / 16 designated