4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
23 companies found
41 designated · 0 approved
14 approved / 34 designated
34 designated · 0 approved
7 designated · 0 approved
7 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
27 approved / 2 designated
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
18 approved / 1 designated
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved