4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
6 companies found
41 designated · 0 approved
1 approved / 25 designated
19 approved / 23 designated
19 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved