4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
15 companies found
70 approved / 109 designated
23 approved / 67 designated
29 approved / 42 designated
8 approved / 27 designated
11 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated
1 designated · 0 approved
2 approved / 1 designated
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved