4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
54 companies found
23 approved / 67 designated
34 approved / 57 designated
10 approved / 43 designated
29 approved / 42 designated
41 designated · 0 approved
34 designated · 0 approved
14 approved / 34 designated
26 approved / 30 designated
28 designated · 0 approved
8 approved / 26 designated
3 approved / 20 designated
19 designated · 0 approved
17 designated · 0 approved
15 designated · 0 approved
13 designated · 0 approved
26 approved / 11 designated
3 approved / 9 designated
9 designated · 0 approved
9 designated · 0 approved
7 designated · 0 approved
7 designated · 0 approved