4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
33 companies found
70 approved / 109 designated
47 approved / 88 designated
23 approved / 67 designated
34 approved / 57 designated
10 approved / 43 designated
39 designated · 0 approved
6 approved / 29 designated
8 approved / 27 designated
3 approved / 15 designated
12 designated · 0 approved
1 approved / 11 designated
11 designated · 0 approved
7 approved / 11 designated
9 designated · 0 approved
9 designated · 0 approved
9 designated · 0 approved
6 designated · 0 approved
1 approved / 5 designated
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved