4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
44 companies found
70 approved / 109 designated
47 approved / 88 designated
10 approved / 43 designated
29 approved / 42 designated
39 designated · 0 approved
34 designated · 0 approved
6 approved / 29 designated
8 approved / 27 designated
8 approved / 26 designated
3 approved / 20 designated
17 designated · 0 approved
3 approved / 15 designated
43 approved / 14 designated
12 designated · 0 approved
11 designated · 0 approved
1 approved / 11 designated
7 approved / 11 designated
9 designated · 0 approved
1 approved / 8 designated
8 designated · 0 approved
5 designated · 0 approved