4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
21 companies found
70 approved / 109 designated
34 approved / 57 designated
9 approved / 23 designated
17 approved / 13 designated
10 designated · 0 approved
2 approved / 8 designated
7 designated · 0 approved
1 approved / 6 designated
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved