4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
8 companies found
41 designated · 0 approved
1 approved / 25 designated
19 designated · 0 approved
81 approved / 8 designated
6 designated · 0 approved
3 approved / 5 designated
4 designated · 0 approved
1 approved / 1 designated