4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
13 companies found
10 approved / 43 designated
29 approved / 42 designated
38 approved / 34 designated
6 approved / 29 designated
8 approved / 27 designated
3 approved / 20 designated
3 approved / 15 designated
12 designated · 0 approved
1 approved / 11 designated
9 designated · 0 approved
5 designated · 0 approved
3 approved / 5 designated
6 approved / 4 designated