4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
10 companies found
23 approved / 67 designated
26 approved / 30 designated
19 designated · 0 approved
9 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved