4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
8 companies found
23 approved / 67 designated
38 approved / 22 designated
18 designated · 0 approved
31 approved / 16 designated
1 approved / 9 designated
7 designated · 0 approved
7 approved / 2 designated
1 designated · 0 approved