4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
24 companies found
47 approved / 88 designated
34 approved / 57 designated
10 approved / 43 designated
29 approved / 42 designated
6 approved / 29 designated
31 approved / 16 designated
10 designated · 0 approved
9 designated · 0 approved
1 approved / 5 designated
5 approved / 4 designated
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved