4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
7 companies found
23 approved / 67 designated
5 approved / 14 designated
7 approved / 4 designated
4 designated · 0 approved
29 approved / 2 designated
1 designated · 0 approved
4 approved / 1 designated