This company develops and markets FDA-approved drugs for rare diseases, with a focus on conditions such as moderate heart failure and benign partial epilepsy, holding one orphan drug designation.
1
Orphan Designations
9
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| AIDS dementia complex | Panretin | Orphan Designation | - |
| AIDS related complex | Panretin | Orphan Designation | - |
| AIDS-related disorder | Panretin | Orphan Designation | - |
| Kaposi's sarcoma | Panretin | Orphan Designation | - |
| benign partial epilepsy of infancy with complex partial seizures | ZONEGRAN | - | FDA Approved |
| moderate heart failure | LANOXIN | - | FDA Approved |
| necrobiosis lipoidica | Panretin | Orphan Designation | - |
| spastic paraplegia-facial-cutaneous lesions syndrome | Panretin | Orphan Designation | - |