2
Orphan Designations
1 approved, 1 designated
2
FDA Approvals
Latest: DIACOMIT (2018)
0
Active Trials
3
Rare Diseases
across 4 areas
0
News (30d)
Quiet
BIOCODEX, INC. is a company with 2 orphan drug designations across 3 rare diseases, including 2 FDA-approved therapies.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| Dravet syndrome | Diacomit | Des.TrialAppr. |
| febrile seizures, familial | Diacomit | Des.TrialAppr. |
| primary hyperoxaluria | Stiripentol | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
2
overlap in 2+ diseases
0/3
candidate diseases
1
avg importance: 70
0
affecting portfolio
0% of portfolio targets high unmet need diseases
2
overlap in 2+ diseases
0/3
candidate diseases
1
avg importance: 70
0
affecting portfolio