1
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| symptomatic form of Coffin-Lowry syndrome in female carriers | Bovine immunoglobulin concentrate, Cryptosporidium parvum | Orphan Designation | - |
| symptomatic form of X-linked centronuclear myopathy in female carriers | Bovine immunoglobulin concentrate, Cryptosporidium parvum | Orphan Designation | - |
| symptomatic form of fragile X syndrome in female carrier | Bovine immunoglobulin concentrate, Cryptosporidium parvum | Orphan Designation | - |
| symptomatic form of hemophilia A in female carriers | Bovine immunoglobulin concentrate, Cryptosporidium parvum | Orphan Designation | - |
| symptomatic form of muscular dystrophy of Duchenne and Becker in female carriers | Bovine immunoglobulin concentrate, Cryptosporidium parvum | Orphan Designation | - |