Comprehensive, easy-to-understand information about this condition
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Kisho delivers this disease record via API, including phenotypes (HPO), genes, orphan drug designations, screening status, and PAG mapping, with version history and governance.
Organizations with orphan designations or approved therapies for this disease
EMD Serono, Inc.
Other
Ebelle D'Ebelle Pharmaceuticals LLC
Other
FoldRx Pharmaceuticals, Inc., a subsidiary of Pfizer Inc.
Other
GalaGen, Inc.
Other
NES Therapeutics, Inc.
Other
Novartis Pharmaceutical Corporation
Other
Orphan Europe SARL
Other
Sandoz Inc
Other
Theravance Biopharma Ireland Limited
Other