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Novartis Pharmaceutical Corporation — Rare Disease Pipeline | Kisho | Kisho
Novartis Pharmaceutical Corporation
Other
8
Orphan Designations
0
FDA Approvals
14
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
B-cell chronic lymphocytic leukemia
Recombinant anti-CD40 monoclonal antibody
Orphan Designation
-
autoimmune lymphoproliferative syndrome
secukinumab
Orphan Designation
-
autoimmune thrombocytopenic purpura
Ianalumab
Orphan Designation
-
chronic inflammatory demyelinating polyradiculoneuropathy
fingolimod
Orphan Designation
-
inborn error of immunity
Ianalumab
Orphan Designation
-
lepromatous leprosy
Lamprene
Orphan Designation
-
micrognathia-recurrent infections-behavioral abnormalities-mild intellectual disability syndrome
secukinumab
Orphan Designation
-
nephrotic syndrome 14
Ianalumab
Orphan Designation
-
non-immunoglobulin-mediated membranoproliferative glomerulonephritis
secukinumab
Orphan Designation
-
ovarian cancer
Patupilone
Orphan Designation
-
plasma cell myeloma
Recombinant anti-CD-40 monoclonal antibody
Orphan Designation
-
symptomatic form of Coffin-Lowry syndrome in female carriers
Cibacalcin
Orphan Designation
-
symptomatic form of fragile X syndrome in female carrier
Cibacalcin
Orphan Designation
-
symptomatic form of hemophilia A in female carriers
Cibacalcin
Orphan Designation
-
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