1
Orphan Designations
0 approved, 1 designated
0
FDA Approvals
5
Active Trials
200 recruiting
7
Rare Diseases
across 12 areas
0
News (30d)
Quiet
IDEAYA Biosciences Inc. is a company with 1 orphan drug designation across 7 rare diseases. Active clinical trials in 5 indications. 1 active policy bill affects their portfolio.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| amyloidosis | - | Des.TrialAppr. |
| breast cancer | - | Des.TrialAppr. |
| cancer | - | Des.TrialAppr. |
| cervical cancer | - | Des.TrialAppr. |
| ocular melanoma | - | Des.TrialAppr. |
| ovarian cancer | - | Des.TrialAppr. |
| uveal melanoma | darovasertib | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
60
overlap in 2+ diseases
0/7
candidate diseases
0
avg importance: 0
1
affecting portfolio
0% of portfolio targets high unmet need diseases
60
overlap in 2+ diseases
0/7
candidate diseases
0
avg importance: 0
1
affecting portfolio