2
Orphan Designations
0 approved, 2 designated
0
FDA Approvals
2
Active Trials
88 recruiting
3
Rare Diseases
across 6 areas
0
News (30d)
Quiet
iOnctura BV is a company with 2 orphan drug designations across 3 rare diseases. Active clinical trials in 2 indications.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| malignant pancreatic neoplasm | Cambritaxestat | Des.TrialAppr. |
| ocular melanoma | - | Des.TrialAppr. |
| uveal melanoma | [6-Fluoro-1-(4-morpholin-4-ylmethyl-phenyl)-5,5-dioxo-4,5-dihydro-1H-5Lambda6-thiochromeno[4,3-c]pyrazol-3-yl]-morpholin-4-yl-methanone hemi-fumarate | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
8
overlap in 2+ diseases
0/3
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
8
overlap in 2+ diseases
0/3
candidate diseases
0
avg importance: 0
0
affecting portfolio