2
Orphan Designations
0 approved, 2 designated
0
FDA Approvals
0
Active Trials
4
Rare Diseases
across 6 areas
0
News (30d)
Quiet
Lam Therapeutics is a company with 2 orphan drug designations across 4 rare diseases.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| heritable pulmonary arterial hypertension | rapamycin | Des.TrialAppr. |
| idiopathic pulmonary arterial hypertension | rapamycin | Des.TrialAppr. |
| lymphangioleiomyomatosis | sirolimus | Des.TrialAppr. |
| pulmonary arterial hypertension | rapamycin | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
14
overlap in 2+ diseases
0/4
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
14
overlap in 2+ diseases
0/4
candidate diseases
0
avg importance: 0
0
affecting portfolio